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Sponsor:
AveXis, Inc.
Location:
Code:
NCT04174157
Conditions
Spinal Muscular Atrophy (SMA)
Eligibility Criteria
Sex: All
Age: 0 - 70+
Healthy Volunteers: Not accepted
Interventions
Prospective observational registry
Zolgensma
Sponsor:
University of Pennsylvania
Location:
Code:
NCT06066957
Conditions
Cytomegalovirus Infections
Transplant-Related Disorder
Eligibility Criteria
Sex: All
Age: 18+
Healthy Volunteers: Not accepted
Interventions
Letermovir 480 MG [Prevymis]