Recruiting
Phase 3

Withdrawal of Tiratricol Treatment in Males with Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)

Sponsor:

Rare Thyroid Therapeutics International AB

Code:

NCT05579327

Conditions

Monocarboxylate Transporter 8 Deficiency

Allan-Herndon-Dudley Syndrome

Eligibility Criteria

Sex: Male

Age: 4+

Healthy Volunteers: Not accepted

Interventions

Tiratricol

Placebo

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information