Recruiting
Phase 3

OAV101

Sponsor:

Novartis Pharmaceuticals

Code:

NCT05335876

Conditions

Spinal Muscular Atrophy (SMA)

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

onasemnogene abeparvovec

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information