Study of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type C

Recruiting

Phase 1

Phase 2

Study of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type CStudy of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type C

Sponsor:

Washington University School of Medicine

Code:

NCT03471143

Conditions

Niemann-Pick Disease, Type C

Eligibility Criteria

Sex: All

Age: 0 - 6

Healthy Volunteers: Not accepted

Interventions

adrabetadex (2-Hydroxypropyl-Beta-Cyclodextrin)

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information

Trial information was received from ClinicalTrials.gov and was last updated on 2025-03-31. This information was provided to ClinicalTrials.gov by Washington University School of Medicine on 2025-03-28.