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Sponsor:
AveXis, Inc.
Location:
Code:
NCT04174157
Conditions
Spinal Muscular Atrophy (SMA)
Eligibility Criteria
Sex: All
Age: 0 - 70+
Healthy Volunteers: Not accepted
Interventions
Prospective observational registry
Zolgensma
Sponsor:
Viking Therapeutics, Inc.
Location:
Code:
NCT04973657
Conditions
Adrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)
Eligibility Criteria
Sex: All
Age: 18+
Healthy Volunteers: Not accepted
Interventions
VK0214
Placebo
Sponsor:
University of Washington
Location:
Code:
NCT06214026
Conditions
Amputation
Eligibility Criteria
Sex: All
Age: 16+
Healthy Volunteers: Not accepted
Interventions
META-Arc foot locked
META-Arc foot unlocked
Sponsor:
Dermavant Sciences, Inc.
Location:
Code:
NCT05172726
Conditions
Plaque Psoriasis
Eligibility Criteria
Sex: All
Age: 2 - 17
Healthy Volunteers: Not accepted
Interventions
tapinarof cream, 1%