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Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

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1

Disulfiram

Recruiting
PHASE1
PHASE2

Sponsor:

University of Washington

Location:

Seattle WA

Code:

NCT05626920

Conditions

Inherited Retinal Dystrophy Primarily Involving Sensory Retina

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

Disulfiram 250 mg

Placebo

N-acetylcysteine

Recruiting
PHASE3

Sponsor:

Johns Hopkins University

Location:

Davis CA, Los Angeles CA, San Francisco CA, Stanford CAshow 21 more

Code:

NCT05537220

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18 - 65

Healthy Volunteers: Not accepted

Interventions

N-acetylcysteine

Placebo

ALK-001

Recruiting
PHASE2

Sponsor:

Alkeus Pharmaceuticals, Inc.

Location:

Los Angeles CA, Gainesville FL, Miami FL, Baltimore MDshow 4 more

Code:

NCT02402660

Conditions

Stargardt Disease

Stargardt Macular Degeneration

Stargardt Macular Dystrophy

Autosomal Recessive Stargardt Disease 1 (ABCA4-related)

Eligibility Criteria

Sex: All

Age: 8 - 70

Healthy Volunteers: Not accepted

Interventions

ALK-001

Placebo

Corticosteroid

Recruiting

Sponsor:

Anne M. Connolly

Location:

Chicago IL, Cincinnati OH, Columbus OH, Dallas TX

Code:

NCT05412394

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 1 - 30

Healthy Volunteers: Not accepted

Interventions

Prednisolone

Myoblasts

Recruiting
PHASE1
PHASE2

Sponsor:

CHU de Quebec-Universite Laval

Location:

Quebec, London

Code:

NCT02196467

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 16+

Healthy Volunteers: Not accepted

Interventions

Myoblast transplantation

Saline injection

Observational Study

Recruiting

Sponsor:

Sumitomo Pharma America, Inc.

Location:

Boston MA

Code:

NCT06517940

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Satralizumab

Recruiting
PHASE2

Sponsor:

Centre Hospitalier Universitaire de Nice

Location:

Ottawa

Code:

NCT06222827

Conditions

Facioscapulohumeral Muscular Dystrophy 1

Eligibility Criteria

Sex: All

Age: 18 - 65

Healthy Volunteers: Not accepted

Interventions

Satralizumab Prefilled Syringe

Placebo Comparator

OCT Guided PTK

Recruiting

Sponsor:

Oregon Health and Science University

Location:

Portland OR

Code:

NCT01243931

Conditions

Corneal Opacity

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

OCT-guided laser phototherapeutic keratectomy

Genetics

Recruiting

Sponsor:

University of Chicago

Location:

Chicago IL

Code:

NCT00138931

Conditions

Cardiomyopathy

Arrhythmia

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

Blood draw (genetic testing)

BS01

Recruiting
PHASE1
PHASE2

Sponsor:

Bionic Sight LLC

Location:

New York NY

Code:

NCT04278131

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

BS01