background image

Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

Filter
1

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

Recruiting

Sponsor:

Sarepta Therapeutics, Inc.

Location:

Phoenix AZ, Little Rock AR, La Jolla CA, Sacramento CAshow 8 more

Code:

NCT04475926

Conditions

Limb-girdle Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 4+

Healthy Volunteers: Not accepted

Trial of Cell Based Therapy for DMD

Recruiting
PHASE1

Sponsor:

Masonic Cancer Center, University of Minnesota

Location:

Minneapolis MN

Code:

NCT06692426

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

MyoPAXon

Tacrolimus

MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby)

Recruiting
PHASE1

Sponsor:

PYC Therapeutics

Location:

Jacksonville FL, Ann Arbor MI, Portland OR, Dallas TXshow 1 more

Code:

NCT06455826

Conditions

Retinitis Pigmentosa 11

Retinal Degeneration

Eye Diseases

Retinal Disease

Retinal Dystrophies

Eligibility Criteria

Sex: All

Age: 12+

Healthy Volunteers: Not accepted

Interventions

VP-001

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients with Duchenne Muscular Dystrophy.

Recruiting

Sponsor:

Catalyst Pharmaceuticals, Inc.

Location:

Little Rock AR, Miami FL, Orlando FL, Chicago ILshow 4 more

Code:

NCT06564974

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 2+

Healthy Volunteers: Not accepted

Interventions

Vamorolone

Promising ROd-cone DYstrophy Gene TherapY

Recruiting
PHASE1
PHASE2

Sponsor:

SparingVision

Location:

Miami FL, Portland OR, Pittsburgh PA

Code:

NCT05748873

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

SPVN06

Genetics of Cardiovascular and Neuromuscular Disease

Recruiting

Sponsor:

University of Chicago

Location:

Chicago IL

Code:

NCT00138931

Conditions

Cardiomyopathy

Arrhythmia

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

Blood draw (genetic testing)

Defining Endpoints in Becker Muscular Dystrophy

Recruiting

Sponsor:

Virginia Commonwealth University

Location:

Orange CA, Aurora CO, Iowa City IA, Kansas City KSshow 5 more

Code:

NCT05257473

Conditions

Becker Muscular Dystrophy

Muscular Dystrophies

Muscular Dystrophy in Children

Muscular Dystrophy, Becker

Eligibility Criteria

Sex: Male

Age: 6+

Healthy Volunteers: Not accepted

Once Weekly Infant Corticosteroid Trial for DMD

Recruiting

Sponsor:

Anne M. Connolly

Location:

Chicago IL, Cincinnati OH, Columbus OH, Dallas TX

Code:

NCT05412394

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 1 - 30

Healthy Volunteers: Not accepted

Interventions

Prednisolone

Phase 2 Tolerability and Effects of ALK-001 on Stargardt Disease

Recruiting
PHASE2

Sponsor:

Alkeus Pharmaceuticals, Inc.

Location:

Los Angeles CA, Gainesville FL, Miami FL, Baltimore MDshow 4 more

Code:

NCT02402660

Conditions

Stargardt Disease

Stargardt Macular Degeneration

Stargardt Macular Dystrophy

Autosomal Recessive Stargardt Disease 1 (ABCA4-related)

Eligibility Criteria

Sex: All

Age: 8 - 70

Healthy Volunteers: Not accepted

Interventions

ALK-001

Placebo

Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy

Recruiting
PHASE1

Sponsor:

Sardocor Corp.

Location:

Kansas City KS, Cincinnati OH, Columbus OH

Code:

NCT06224660

Conditions

DMD-Associated Dilated Cardiomyopathy

Eligibility Criteria

Sex: Male

Age: 18+

Healthy Volunteers: Not accepted

Interventions

SRD-001