background image

Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

Filter
1

BrainGate2

Recruiting

Sponsor:

Leigh R. Hochberg, MD, PhD.

Location:

Stanford CA, Boston MA

Code:

NCT05724173

Conditions

Anarthria

Dysarthria

Tetraplegia

Spinal Cord Injuries

Amyotrophic Lateral Sclerosis

Eligibility Criteria

Sex: All

Age: 18 - 70+

Healthy Volunteers: Not accepted

Interventions

BrainGate Neural Interface System

BS01

Recruiting
PHASE1
PHASE2

Sponsor:

Bionic Sight LLC

Location:

New York NY

Code:

NCT04278131

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

BS01

RODY Gene Therapy

Recruiting
PHASE1
PHASE2

Sponsor:

SparingVision

Location:

Miami FL, Portland OR, Pittsburgh PA

Code:

NCT05748873

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

SPVN06

BB-301

Recruiting
PHASE1
PHASE2

Sponsor:

Benitec Biopharma, Inc.

Location:

New York NY

Code:

NCT06185673

Conditions

Oculopharyngeal Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 65

Healthy Volunteers: Not accepted

Interventions

BB-301: Dose escalation phase 1b cohort 1

BB-301: Dose escalation phase 1b cohort 2

BB-301: Dose escalation phase 1b cohort 3

BB-301: Dose expansion phase 2a

OCT Guided PTK

Recruiting

Sponsor:

Oregon Health and Science University

Location:

Portland OR

Code:

NCT01243931

Conditions

Corneal Opacity

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

OCT-guided laser phototherapeutic keratectomy

Exercise

Recruiting

Sponsor:

Massachusetts General Hospital

Location:

Boston MA

Code:

NCT06716931

Conditions

Myotonic Dystrophy 2

Eligibility Criteria

Sex: All

Age: 18 - 70

Healthy Volunteers: Not accepted

Interventions

Exercise

INS1201

Recruiting
PHASE1

Sponsor:

Insmed Gene Therapy LLC

Location:

Atlanta GA

Code:

NCT06817382

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 2 - 4

Healthy Volunteers: Not accepted

Interventions

INS1201

Low-Dose Naltrexone

Recruiting

Sponsor:

Stanford University

Location:

Palo Alto CA

Code:

NCT02502162

Conditions

Complex Regional Pain Syndrome

Eligibility Criteria

Sex: All

Age: 18 - 70

Healthy Volunteers: Not accepted

Interventions

LDN

Placebo

Reactive Oxygen Species

Recruiting
PHASE2

Sponsor:

Massachusetts Eye and Ear Infirmary

Location:

Boston MA

Code:

NCT04440280

Conditions

Fuchs Endothelial Corneal Dystrophy

Eligibility Criteria

Sex: All

Age: 21+

Healthy Volunteers: Not accepted

Interventions

N-acetyl cysteine (NAC) 10% solution

N-acetyl cysteine (NAC) 20% solution

Visine Dry Eye Relief eye drops

Genetics

Recruiting

Sponsor:

University of Chicago

Location:

Chicago IL

Code:

NCT00138931

Conditions

Cardiomyopathy

Arrhythmia

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

Blood draw (genetic testing)