Recruiting

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

Sponsor:

AveXis, Inc.

Code:

NCT04174157

Conditions

Spinal Muscular Atrophy (SMA)

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

Prospective observational registry

Zolgensma

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information